With double-digit annual growth in the global gene therapy market, people with the skills to treat or prevent disease through experimental gene techniques have never been in higher demand. This course brings you closer to the exciting discoveries in genetics by providing a foundational survey of the existing technology for gene editing and helps you understand the tools of discovery.

Skills Needed

• prior molecular biology coursework or background is strongly recommended.

Learning Outcomes

At the conclusion of the course, you should be able to

• Understand the current technologies used in gene therapy treatments for human disease
• Understand why each technology is used in gene therapy and how the technology was developed.
• Understand how the whole process works for each of the covered topics, including what reagents are used and the editing process.
• Learn how to pick guide RNAs from sequences using CRISPR

Topics Include

• Gene therapy landscape overview
• Uses of viruses in gene therapy
• RNAi
• Car-T gene therapy
• CRISPR gene therapy

Notes

This class offers a detailed analysis of the biology underlying each technology and analyzes the advantages,disadvantages, and limitations of each.